News

Scientists have learned more about the structure of the collagen 6 protein and how muscular dystrophy-causing mutations affect it.
Columnist Shalom Lim will continue to pursue the themes that matter to him as a person with Duchenne MD, but as a writer now, ...
Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational therapy SRP-1003 in DM1.
Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational therapy SRP-1003 in DM1.
Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.
Columnist Robin Stemple, his brothers, and more enjoy a long-in-the works family music celebration at his mother's nursing home.
A protein called MYOD has long been known to be able to turn on genes, but a recent study has found that it also can turn off ...
Enrollment is now ongoing in a first-in-human clinical trial testing EPI-321, a therapy designed to target the underlying ...