News

Scientists have learned more about the structure of the collagen 6 protein and how muscular dystrophy-causing mutations affect it.
Columnist Shalom Lim will continue to pursue the themes that matter to him as a person with Duchenne MD, but as a writer now, ...
Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational therapy SRP-1003 in DM1.
Preliminary data are expected this year for a Phase 1/2 clinical trial testing the investigational therapy SRP-1003 in DM1.
Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.
A protein called MYOD has long been known to be able to turn on genes, but a recent study has found that it also can turn off ...
Enrollment is now ongoing in a first-in-human clinical trial testing EPI-321, a therapy designed to target the underlying ...
Columnist Shalom Lin and his partner, Amanda — both disabled artists — find that their challenges are exactly what can drive ...