Lasting gains in swallowing ability have been reported for four people with oculopharyngeal muscular dystrophy given gene therapy in a trial.

Columnist Shalom Lim has discovered that a personal sense of belonging is built through simple presence. Art can help foster ...

Dosing has begun in a Phase 2 clinical trial testing the experimental oral therapy SAT-3247 in boys with Duchenne muscular ...

Guest writer Matthew Busch says that, despite the setbacks and surgeries he's endured, he's now thriving in life with Duchenne MD.

An honest answer about her sons would mean talking about all the things Duchenne MD has taken from them, writes columnist.

A clinical trial testing Duchenne gene-editing therapy candidate PBGENE-DMD will soon launch in the U.S., having won ...

Dangerous snow and ice, along with FSHD symptoms, made it impossible for columnist Robin Stemple to leave his home for two weeks.

A Phase 3 clinical trial testing SGT-003, a gene therapy candidate for Duchenne muscular dystrophy (DMD), will start dosing ...

When faced with a bad moment or adverse event, columnist Patrick Moeschen says it helps to remember the rule of 10.

The U.S. Food and Drug Administration (FDA) has granted fast track designation to Dyscorban (ifetroban), Cumberland Pharmaceuticals’ treatment candidate for heart problems in Duchenne muscular ...

I’d like to share my thoughts on what the word “strength” means. The United States has had one president who used a wheelchair: Franklin D. Roosevelt. During his time in the political spotlight, he ...