7 Rare Diseases That Can Now Be Treated
interestingengineering.com
7 Rare Diseases That Can Now Be Treated
There are many rare disease out there that currently have no cure or treatment. Thankfully these seven can be crossed off that list.
Mar 3, 2019
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🗓️ Tuesday, February 24 at 9:30am 📍 Big Night Live, Boston | Virtual options also available Through discussions and stories, Rare Disease Summit will spotlight innovation across drug development, diagnostics, funding, and policy – while centering the voices of patients and caregivers driving change alongside industry and research leaders. Speakers include: ✅ Dr. Wendy Chung, Chief of Pediatrics, Boston Children's Hospital ✅ Kristen DeAndrade, Founder and Executive Director, Little Legs Big Hea
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121K views · 1.1K reactions | 7-year-old Luciana Wilken has fibrodysplasia ossificans progressiva (FOP), a very rare genetic disorder causing muscles and tendons to turn into bone. A mother recounts the moment she connected her daughter's symptoms to this rare disease after watching a documentary. It was like a jigsaw, she says, putting all the pieces together. #FOP #GeneticDisorder #RareDisease #MedicalMystery #Inspiration #Hope | Real Stories | Facebook
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